Prion Disease Treatment: A Milestone in Gene Therapy

April 7, 2025

As researchers race towards breakthroughs in prion disease treatment, the urgency is underscored by the devastating effects of such conditions.Prion diseases, including notorious variants like Creutzfeldt-Jakob disease and fatal familial insomnia, devastate brain function through misfolded prion proteins, leading to severe neurodegeneration.
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